No abstract available
Publication types
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Research Support, U.S. Gov't, P.H.S.
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Review
MeSH terms
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Animals
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Enzymes / deficiency*
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Enzymes / genetics
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Genetic Therapy
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Humans
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Lysosomes / enzymology*
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Metabolism, Inborn Errors / enzymology*
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Metabolism, Inborn Errors / therapy
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Mutation