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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2002 3
2003 3
2004 1
2005 4
2006 4
2007 1
2008 6
2009 8
2010 8
2011 10
2012 7
2013 8
2014 11
2015 10
2016 7
2017 9
2018 1
2019 5
2020 3
2021 3
2022 2
2023 2
2024 0

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103 results

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Page 1
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.
Mendell JR, Al-Zaidy S, Shell R, Arnold WD, Rodino-Klapac LR, Prior TW, Lowes L, Alfano L, Berry K, Church K, Kissel JT, Nagendran S, L'Italien J, Sproule DM, Wells C, Cardenas JA, Heitzer MD, Kaspar A, Corcoran S, Braun L, Likhite S, Miranda C, Meyer K, Foust KD, Burghes AHM, Kaspar BK. Mendell JR, et al. Among authors: kaspar bk. N Engl J Med. 2017 Nov 2;377(18):1713-1722. doi: 10.1056/NEJMoa1706198. N Engl J Med. 2017. PMID: 29091557 Free article. Clinical Trial.
Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS.
Bravo-Hernandez M, Tadokoro T, Navarro MR, Platoshyn O, Kobayashi Y, Marsala S, Miyanohara A, Juhas S, Juhasova J, Skalnikova H, Tomori Z, Vanicky I, Studenovska H, Proks V, Chen P, Govea-Perez N, Ditsworth D, Ciacci JD, Gao S, Zhu W, Ahrens ET, Driscoll SP, Glenn TD, McAlonis-Downes M, Da Cruz S, Pfaff SL, Kaspar BK, Cleveland DW, Marsala M. Bravo-Hernandez M, et al. Among authors: kaspar bk. Nat Med. 2020 Jan;26(1):118-130. doi: 10.1038/s41591-019-0674-1. Epub 2019 Dec 23. Nat Med. 2020. PMID: 31873312 Free PMC article.
High content analysis in amyotrophic lateral sclerosis.
Rinaldi F, Motti D, Ferraiuolo L, Kaspar BK. Rinaldi F, et al. Among authors: kaspar bk. Mol Cell Neurosci. 2017 Apr;80:180-191. doi: 10.1016/j.mcn.2016.12.001. Epub 2016 Dec 11. Mol Cell Neurosci. 2017. PMID: 27965018 Free PMC article. Review.
Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates.
Powers S, Likhite S, Gadalla KK, Miranda CJ, Huffenberger AJ, Dennys C, Foust KD, Morales P, Pierson CR, Rinaldi F, Perry S, Bolon B, Wein N, Cobb S, Kaspar BK, Meyer KC. Powers S, et al. Among authors: kaspar bk. Mol Ther. 2023 Sep 6;31(9):2767-2782. doi: 10.1016/j.ymthe.2023.07.013. Epub 2023 Jul 22. Mol Ther. 2023. PMID: 37481701 Free article.
Over the barrier and through the blood: to CNS delivery we go.
Foust KD, Kaspar BK. Foust KD, et al. Among authors: kaspar bk. Cell Cycle. 2009 Dec 15;8(24):4017-8. doi: 10.4161/cc.8.24.10245. Epub 2009 Dec 5. Cell Cycle. 2009. PMID: 19949299 Free PMC article. No abstract available.
Gene-targeted therapies for the central nervous system.
Miller TM, Smith RA, Kordasiewicz H, Kaspar BK. Miller TM, et al. Among authors: kaspar bk. Arch Neurol. 2008 Apr;65(4):447-51. doi: 10.1001/archneur.65.4.nnr70007. Epub 2008 Feb 11. Arch Neurol. 2008. PMID: 18268183 Review. No abstract available.
103 results