Research Articles, Neurobiology of Disease
Single Systemic Administration of a Gene Therapy Leading to Disease Treatment in Metachromatic Leukodystrophy Arsa Knockout Mice
Thia St. Martin, Tania A. Seabrook, Katherine Gall, Jenn Newman, Nancy Avila, April Hayes, Monicah Kivaa, Jason Lotterhand, Michael Mercaldi, Kruti Patel, Jose Israel Rivas, Stephen Woodcock, Teresa L. Wright, Albert B. Seymour, Omar L. Francone and Jacinthe Gingras
Journal of Neuroscience 28 March 2023, JN-RM-1829-22; DOI: https://doi.org/10.1523/JNEUROSCI.1829-22.2023